Abstract Details

Title rAAV5 Mediated Delivery of Dysferlin as a Therapeutic Strategy for LGMD2B and Miyoshi Myopathy

Topic Muscle Disease/Neuromuscular Junction

Presentation(s) (-)

Poster/Presentation
Number 001

Background

Objective

Design/Methods

Results

Conclusions

Authors/Disclosures
Louise R. Rodino-Klapac (Sarepta Therapeutics)	Ms. Rodino-Klapac has received personal compensation for serving as an employee of Sarepta Therapeutics, Inc.. Ms. Rodino-Klapac has received stock or an ownership interest from Sarepta Therapeutics. Ms. Rodino-Klapac has received intellectual property interests from a discovery or technology relating to health care.
	No disclosure on file
	No disclosure on file
Vinod Malik (Nationwide Childrens Hospital)	No disclosure on file
	No disclosure on file
	No disclosure on file
	No disclosure on file
K. Reed Clark, PhD	No disclosure on file
Robert H. Brown, Jr., MD, DPhil (Univ of Massachusetts Medical School)	Dr. Brown has received personal compensation for serving as an employee of ApicBio. Dr. Brown has received personal compensation in the range of $10,000-$49,999 for serving as a Consultant for ApicBio. Dr. Brown has received personal compensation in the range of $10,000-$49,999 for serving as an officer or member of the Board of Directors for Warren Alpert Foundation. Dr. Brown has received stock or an ownership interest from ApicBio. Dr. Brown has received stock or an ownership interest from Amylx. Dr. Brown has received stock or an ownership interest from Imstar. The institution of Dr. Brown has received research support from Angel Fund for ALS Research. The institution of Dr. Brown has received research support from ALS Association. The institution of Dr. Brown has received research support from ALSOne. The institution of Dr. Brown has received research support from NINDS. The institution of Dr. Brown has received research support from ALS Finding A Cure. Dr. Brown has received publishing royalties from a publication relating to health care.
Jerry S. Mendell, MD (Univ of Texas Health Science)	No disclosure on file