Abstract Details

Title Development of Biomarkers for HDAC Inhibitor Treatment of Friedreich[apos]s Ataxia

Topic Neurogenetics and Gene Therapy

Presentation(s) (-)

Poster/Presentation
Number 010

Background

Objective

Design/Methods

Results

Conclusions

Authors/Disclosures
Massimo Pandolfo, MD, FAAN (Montreal Neurological Institute/Hospital)	Dr. Pandolfo has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Minoryx. Dr. Pandolfo has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Design Therapeutics . Dr. Pandolfo has received personal compensation in the range of $5,000-$9,999 for serving as a Consultant for Reata. Dr. Pandolfo has received personal compensation in the range of $5,000-$9,999 for serving as a Consultant for Biomarin. Dr. Pandolfo has received personal compensation in the range of $5,000-$9,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Design Therapeutics. Dr. Pandolfo has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Larimar. Dr. Pandolfo has received personal compensation in the range of $5,000-$9,999 for serving as an Editor, Associate Editor, or Editorial Advisory Board Member for Neurology Genetics. Dr. Pandolfo has stock in Voyager Therapeutics. The institution of Dr. Pandolfo has received research support from Freidreich Ataxaia Research Alliance. Dr. Pandolfo has a non-compensated relationship as a Scientific Advisory Board with Friedreich Ataxia Research Alliance that is relevant to AAN interests or activities. Dr. Pandolfo has a non-compensated relationship as a Member-Meeting Management Committee with AAN that is relevant to AAN interests or activities.
Lila E. Sheikhi, MD (Hawthorn Health, LLC)	Dr. Sheikhi has nothing to disclose.
	No disclosure on file
Myriam Rai	No disclosure on file
	No disclosure on file
	No disclosure on file
	No disclosure on file
	No disclosure on file
David R. Lynch, MD, PhD (Children's Hospital of Philadelphia)	The institution of Dr. Lynch has received research support from reata. The institution of Dr. Lynch has received research support from PTC. Dr. Lynch has received intellectual property interests from a discovery or technology relating to health care.
	No disclosure on file