2010 Annual Meeting | Anterior Horn: Spinal Muscular Atrophy

Date Wednesday 04/14/10

Time 04:15 PM - 05:30 PM Add To Calendar

Session Format This program will be presented both in-person and online

On Demand This program is not expected to be available in the meeting's On Demand product.

Event Type Scientific Platform Session

Topic(s) Anterior Horn

CME Available No CME available

Event Timeline
04:15 PM - 05:30 PM	Abstract	001 - Maximum Ulnar Compound Motor Action Potential (CMAP) Is Related to Motor Function in Children with Spinal Muscular Atrophy: Report from the SMA CARNI-VAL Clinical Trial
04:15 PM - 05:30 PM	Abstract	002 - SMN Transcript Quantification as a Surrogate Outcome Measure in Spinal Muscular Atrophy (SMA) Clinical Trials: Towards a Validated International Standard Operating Procedure (SOP)
04:15 PM - 05:30 PM	Abstract	003 - Segmental Thigh Muscle Volumes Estimated by Magnetic Resonance Imaging (MRI) Remain Stable over a Six Month Interval in Spinal Muscular Atrophy (SMA): An Effective Early Biomarker?
04:15 PM - 05:30 PM	Abstract	004 - Dominantly-Inherited Spinal Muscular Atrophy with Lower Limb Predominance Showing Linkage to 14q32
04:15 PM - 05:30 PM	Abstract	005 - Investigating the Cellular Site of Action of Survival Motor Neuron Protein

Faculty Disclosures
Brian K. Kaspar, PhD	No disclosure on file
Charlotte J. Sumner, MD, FAAN	Dr. Sumner has received personal compensation for serving as an employee of Biogen. Dr. Sumner has received personal compensation for serving as an employee of Avexis. Dr. Sumner has received personal compensation for serving as an employee of Roche/Genentech. Dr. Sumner has received personal compensation for serving as an employee of Ionis Pharmaceuticals. Dr. Sumner has received personal compensation for serving as an employee of Sarepta. Dr. Sumner has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Biogen. Dr. Sumner has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Avexis/Novartis. Dr. Sumner has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Roche/Genentech. Dr. Sumner has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Sarepta. Dr. Sumner has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Alnylam. Dr. Sumner has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Proneurotech. Dr. Sumner has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for CMTRF. Dr. Sumner has received personal compensation in the range of $500-$4,999 for serving as an Editor, Associate Editor, or Editorial Advisory Board Member for Journal Clinical Investigation. Dr. Sumner has received research support from Roche. Dr. Sumner has received intellectual property interests from a discovery or technology relating to health care. Dr. Sumner has received publishing royalties from a publication relating to health care.
John T. Kissel, MD, FAAN	Dr. Kissel has nothing to disclose.
Gyula Acsadi, MD, FAAN	Dr. Acsadi has received personal compensation in the range of $5,000-$9,999 for serving as a Consultant for Biogen. Dr. Acsadi has received personal compensation in the range of $5,000-$9,999 for serving as a Consultant for Avexis. Dr. Acsadi has received personal compensation in the range of $5,000-$9,999 for serving as a Consultant for Serepta. Dr. Acsadi has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Genentech. Dr. Acsadi has received personal compensation in the range of $5,000-$9,999 for serving on a Speakers Bureau for Biogen.
Bakri Elsheikh, MD, FAAN	Dr. Elsheikh has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Biogen . Dr. Elsheikh has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Argnex . The institution of Dr. Elsheikh has received research support from Biogen. The institution of Dr. Elsheikh has received research support from Cure SMA.
	No disclosure on file
Thomas O. Crawford, MD	Dr. Crawford has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Biogen.
Aga J. Lewelt	No disclosure on file
Julaine M. Florence	Ms. Florence has nothing to disclose.
Matthew Harms, MD	Dr. Harms has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Biogen. Dr. Harms has received personal compensation in the range of $50,000-$99,999 for serving as a Consultant for Muscular Dystrophy Association. Dr. Harms has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Invitae. Dr. Harms has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Variant Bio. Dr. Harms has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Sarepta. Dr. Harms has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Amylyx. Dr. Harms has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for uniQure. Dr. Harms has received personal compensation in the range of $5,000-$9,999 for serving as an Expert Witness for Littlepage Booth. Dr. Harms has received personal compensation in the range of $500-$4,999 for serving as an Expert Witness for O'Connor First. Dr. Harms has received personal compensation in the range of $500-$4,999 for serving as an Expert Witness for Searcy Denney. Dr. Harms has received personal compensation in the range of $500-$4,999 for serving as an Expert Witness for Ford, Parshall & Baker LLC . The institution of Dr. Harms has received research support from ALS Association. The institution of Dr. Harms has received research support from Ionis. The institution of Dr. Harms has received research support from ALS Finding a Cure. The institution of Dr. Harms has received research support from Target ALS.
Alan Pestronk, MD, FAAN	The institution of Dr. Pestronk has received research support from RA. The institution of Dr. Pestronk has received research support from Fulcrum. The institution of Dr. Pestronk has received research support from Acceleron. The institution of Dr. Pestronk has received research support from Biogen. The institution of Dr. Pestronk has received research support from Jain. The institution of Dr. Pestronk has received research support from Sanofi. The institution of Dr. Pestronk has received research support from Muscular Dystrophy Association. Dr. Pestronk has received intellectual property interests from a discovery or technology relating to health care.
J. Americo M. Fernandes, Jr., MD, FAAN	Dr. Fernandes has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Columbia University. The institution of Dr. Fernandes has received research support from MGH philanthropy (Clene, Seelos, UCB, Biohaven, Prilenia, Denali Therapeutics, Calico Life Sciences. The institution of Dr. Fernandes has received research support from Columbia University. The institution of Dr. Fernandes has received research support from PTC Therapeutics. The institution of Dr. Fernandes has received research support from Clene.
Sandra P. Reyna, MD	Dr. Reyna has received personal compensation for serving as an employee of Novartis Gene Therapies.
Robert H. Baloh, MD, PhD, FAAN	Dr. Baloh has received personal compensation for serving as an employee of Roche. Dr. Baloh has received personal compensation in the range of $0-$499 for serving on a Scientific Advisory or Data Safety Monitoring board for Acurastem. Dr. Baloh has received personal compensation in the range of $10,000-$49,999 for serving as an Expert Witness for Irell. The institution of Dr. Baloh has received research support from NIH and CIRM.
Robert Gardner, Jr., MD	No disclosure on file
Kathryn J. Swoboda, MD	Dr. Swoboda has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Biogen. Dr. Swoboda has received personal compensation in the range of $500-$4,999 for serving on a Speakers Bureau for Biogen. The institution of Dr. Swoboda has received research support from Biogen.
Louise R. Simard, PhD	No disclosure on file
Muhammad Al-Lozi, MD	Dr. Al-Lozi has nothing to disclose.
Umrao R. Monani, PhD	No disclosure on file
Gyu Hwan Park, MD	No disclosure on file
Mary K. Schroth, MD	Dr. Schroth has received personal compensation for serving as an employee of Cure SMA. The institution of Dr. Schroth has received personal compensation in the range of $5,000-$9,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Biogen. The institution of Dr. Schroth has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Roche. The institution of Dr. Schroth has received research support from Biogen.
Megan Montgomery	No disclosure on file
Omar A. Danoun, MD	Dr. Danoun has nothing to disclose.
Shishir K. Rao, MD	The institution of Dr. Rao has received research support from Eisai, Inc.
Adam Witt, MD	No disclosure on file
Valerie Sim, MD, BSc	The institution of Dr. Sim has received research support from the CJD Foundation. The institution of Dr. Sim has received research support from National Research Council of Canada Nanotechnology Research Centre. Dr. Sim has received intellectual property interests from a discovery or technology relating to health care.
Melissa Sorosina	No disclosure on file